Machado Joseph Disease Treatment Market Outlook & Emerging Therapies
1. Executive Summary The Machado-Joseph Disease (MJD), or Spinocerebellar Ataxia Type 3 (SCA3), treatment market is currently driven by symptomatic management but is on the cusp of significant transformation due to a robust pipeline of disease-modifying therapies (DMTs). MJD is the most common autosomal dominant ataxia, caused by a CAG repeat expansion in the ATXN3 gene. The global Machado...
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